A method for arrayed CRISPRi screening in organoids enables the investigation of morphogenesis in human stem cell-derived tissues, revealing the roles of ZIC2, SOX11, and ZNF521 in neural tube closure ...
Casgevy sickle cell gene therapy is now FDA-approved for children as young as two, opening access for 5,500 more U.S. kids.
Objectives Treatment of rheumatoid arthritis (RA) relies on immunomodulatory drugs that can compromise immunity, inducing secondary immunodeficiency (SID). However, features of SID, such as ...
The study reveals that prenatal fructose exposure directly alters neural stem cells (NSCs), the foundational master cells ...
A handful of start-up firms are testing therapies that target specific epigenetic markers to treat everything from high ...
Reproductive history genetic health risk is deeper than lifestyle choices. A FinnGen preprint posted June 9, 2026 finds that ...
Synonymous DNA substitutions have often been viewed as quiet changes because they do not alter the amino acid sequence of a ...
Chinese Academy of Agricultural Sciences team decodes 118 chromosomes of key cultivar POJ2878 to reveal sucrose storage ...
Discover how high estrogen levels may impact trauma resilience, based on recent research exploring hormonal influence on mental health and recovery.
Pharmaceutical Technology on MSN
UniQure to seek approval of Huntington’s gene therapy after FDA U-turn
uniQure confirmed it will submit its BLA in Q3 2026, though there is still a required confirmatory study to conduct.
Before the advent of modern life saving medicines, the immune system protected human beings from deadly pathogens and foreign objects for thousands of years. Given that the diversity of pathogens and ...
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